NCT02530905
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- David Geffen School of Medicine at UCLA Los Angeles, California, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Kennedy Krieger Institute Baltimore, Maryland, United States