NCT02246478
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- National Center of Neurology and Psychiatry Tokyo, Japan
Clinical trial condition
Genetic Diseases, X-Linked
Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.
1,244 public trials
227 recruiting studies
Genetic Diseases, X-Linked trial results
NCT01347242
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
-
- Great Ormond Street Hospital London, United Kingdom
- Royal Free Hospital London, United Kingdom
NCT01210196
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- ZNA Middelheim Antwerp, Belgium
- Institute of Pathology et de Génétique (IPG) Gosselies, Belgium
- Charles University in Prague and General University Hospital in Prague Prague, Czechia
- National University Hospital, Rigshospitalet Copenhagen, Denmark
Completed
Long-term Extension Study to Assess Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)
NCT03038399
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- University of California Davis Davis, California, United States
- University of Florida Gainesville, Florida, United States
- Nemours Children's Hospital Orlando, Florida, United States
- Ann & Robert H. Lurie Children's Hospital Chicago, Illinois, United States
NCT02418793
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
- Locations
-
- City of Hope Duarte, California, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
- Orthopaedic Hemophilia Treatment Center Los Angeles, California, United States
- University of California Davis Medical Center Sacramento, California, United States
Completed
BAX 326 Pediatric Study
NCT01488994
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
- Locations
-
- LNJP Maulana Azad Medical College & Associated Hospitals New Delhi, India
- University Pediatric Hospital Krakow, Poland
- Stanislaw Popowski Provincial Specialist Pediatric Hospital Olsztyn, Poland
- Professor Tadeusz Sokolowski Independent Public Teaching Hospital of the Pomeranian Medical University in Szczecin Szczecin, Poland
Completed
BAX 326 (rFIX) Continuation Study
NCT01286779
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
- Locations
-
- Instituto de Hematología y Medicina Clíncia Rubén Dávoli Rosario, Argentina
- UNIFESP - Universidade Estadual de Sao Paulo São Paulo, Brazil
- Specialized Haematological Hospital "Joan Pavel" Sofia, Bulgaria
- Hospital Dr. Sotero del Rio Santiago, Chile
Completed
Pivotal Study (Pharmacokinetics, Efficacy, Safety) of BAX 326 (rFIX) in Hemophilia B Patients
NCT01174446
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
- Locations
-
- Rosario, Argentina
- Brasília, Brazil
- São Paulo, Brazil
- Sofia, Bulgaria
NCT01507896
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
- Locations
-
- Instituto de Hematología y Medicina Clínica Rubén Dávoli Rosario, Argentina
- Specialized Haematological Hospital "Joan Pavel" Sofia, Bulgaria
- Hospital Dr. Sotero del Rio Santiago, Chile
- Centro Medico Imbanaco Cali, Colombia
NCT00851721
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +9 more
- Locations
-
- Chicago, Illinois, United States
- Cleveland, Ohio, United States
- Rio de Janeiro, Brazil
- São Paulo, Brazil