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Clinical trial condition

Muscular Disorders, Atrophic

Explore clinical trials studying Muscular Disorders, Atrophic. Study availability and eligibility vary by location and protocol.

628 public trials 120 recruiting studies
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Muscular Disorders, Atrophic trial results

Recruiting

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

NCT07486934

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +18 more
Locations
  • UCSD - Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • IU Health Neuroscience Center Indianapolis, Indiana, United States
  • Roy Blunt NextGen Precision Health Institute Columbia, Missouri, United States
View all 39 locations
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Recruiting

The Efficacy and Safety of Once Daily Mexiletine PR in Patients With Myotonic Dystrophy Type 1 and Type 2

NCT06523400

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +9 more
Locations
  • Laboratory for Muscle Diseases and Neuropathies Leuven, Belgium
  • Aarhus University Hospital Aarhus, Denmark
  • Ludug-Maximilians University München, Germany
  • Azienda Ospedaliera Universitaria Policlinico Tor Vergata Rome, Italy
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Recruiting

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

NCT06564974

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Childrens Hospital Little Rock, Arkansas, United States
  • Loma Linda University Pediatric Subspecialty Clinics Loma Linda, California, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
View all 33 locations
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Recruiting

Study of Inherited Neurological Disorders

NCT00004568

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Motor Neuron Disease, +11 more
Locations
  • National Institutes of Health Clinical Center Bethesda, Maryland, United States
  • University of Mali Bamako, Mali
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Recruiting

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

NCT06844214

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +9 more
Locations
  • University of Florida, 2004 Mowry Road - Site Number: 8400005 Gainesville, Florida, United States
  • University of South Florida - Neuromuscular Research, 13330 USF Laurel Drive - Site Number: 8400001 Tampa, Florida, United States
  • Columbia University Medical Center - Neurological Institute, 710 W. 168th, 2nd floor, suite 204 - Site Number : 8400003 New York, United States
  • Hospital Italiano de Buenos Aires, Juan Domingo Peron 4190 - Site Number: 0320001 Buenos Aires, Argentina
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Recruiting

Observatoire Des Patients Atteints de Laminopathies et Emerinopathies (Observatory for PAtients With Laminopathies and Emerinopathies)

NCT03058185

Conditions
Autosomal Emery-Dreifuss Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Emerinopathies, +11 more
Locations
  • Centre de référence maladies neuromusculaires,CHU d'Angers Angers, France
  • CHU Strasbourg Strasbourg, Bas-Rhin, France
  • CHU Marseille Marseille, Bouches-du-Rhône, France
  • CHU Caen Caen, Calvados, France
View all 29 locations
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Recruiting

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

NCT07287189

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +10 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Colorado Children's Aurora, Colorado, United States
  • Lurie Children's Chicago, Illinois, United States
  • UMass Memorial Medical Center Worcester, Massachusetts, United States
View all 21 locations
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Recruiting

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

NCT04626674

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Stanford University Palo Alto, California, United States
  • University of California, Davis Sacramento, California, United States
  • Washington University in St. Louis St Louis, Missouri, United States
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