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Clinical trial condition

Congenital, Hereditary, and Neonatal Diseases and Abnormalities

Explore clinical trials studying Congenital, Hereditary, and Neonatal Diseases and Abnormalities. Study availability and eligibility vary by location and protocol.

18,481 public trials 3,141 recruiting studies
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Congenital, Hereditary, and Neonatal Diseases and Abnormalities trial results

Recruiting

External Multicenter Validation of the APTTO Model for Prolonged APTT Using Clot Waveform Analysis

NCT07418099

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Blood Platelet Disorders, +12 more
Locations
  • Hospital Universitario Severo Ochoa Leganés, Madrid, Spain
  • Hospital de la Santa Creu i Sant Pau Barcelona, Spain
  • Hospital Universitario Arnau De Vilanova Lleida, Spain
  • Hospital Universitario 12 de Octubre Madrid, Spain
View all 16 locations
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Recruiting

Efficacy and Safety of Mibavademab in Adult and Pediatric Patients With Generalized Lipodystrophy

NCT07220785

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Generalized Lipodystrophy, Genetic Diseases, Inborn, +12 more
Locations
  • University of Michigan Ann Arbor, Michigan, United States
  • UT Southwestern Medical Center Dallas, Texas, United States
  • Assistance Publique-Hopitaux de Paris (AP-HP) Paris, France
  • Hopital Universitaire Robert-Debre Paris, France
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Recruiting

Treatment of Obstructive Sleep Apnea With Personalized Surgery in Children With Down Syndrome (TOPS-DS)

NCT05508971

Conditions
Abnormalities, Multiple, Apnea, Chromosome Disorders, +16 more
Locations
  • Colorado Children's Hospital Aurora, Colorado, United States
  • University of Michigan Ann Arbor, Michigan, United States
  • Cincinnati Children's Hospital Cincinnati, Ohio, United States
  • Oregon Health and Science University Portland, Oregon, United States
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Recruiting

Baby ABS (Abdominal Binder Study)

NCT07049900

Conditions
Bronchopulmonary Dysplasia, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases and Pregnancy Complications, +15 more
Locations
  • University of Minnesota Minneapolis, Minnesota, United States
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Recruiting

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

NCT04626674

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Stanford University Palo Alto, California, United States
  • University of California, Davis Sacramento, California, United States
  • Washington University in St. Louis St Louis, Missouri, United States
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Recruiting

A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B

NCT06379789

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Orthopaedic Hemophilia Treatment Center Los Angeles, California, United States
  • David Geffen School of Medicine at UCLA Los Angeles, California, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • University of California Davis Sacramento, California, United States
View all 49 locations
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Recruiting

A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A

NCT05987449

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +6 more
Locations
  • UC Davis Cancer Center Sacramento, California, United States
  • Georgetown Uni Medical Center Washington D.C., District of Columbia, United States
  • Indiana Hemophilia & Thrombosis center Indianapolis, Indiana, United States
  • University of Iowa Hospitals and Clnics Dept of Pediatrics Iowa City, Iowa, United States
View all 14 locations
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Recruiting

Testing for Safety and Colorectal Cancer Preventive Effects of ONC201

NCT05630794

Conditions
Adenoma, Adenomatous Polyposis Coli, Adenomatous Polyps, +21 more
Locations
  • University of Michigan Rogel Cancer Center Ann Arbor, Michigan, United States
  • Washington University School of Medicine St Louis, Missouri, United States
  • Cleveland Clinic Foundation Cleveland, Ohio, United States
  • Ohio State University Comprehensive Cancer Center Columbus, Ohio, United States
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Recruiting

A Dose-ranging Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Galvokimig in Adult Study Participants With Atopic Dermatitis

NCT07277660

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Atd002 52021 Oceanside, California, United States
  • Atd002 52008 Santa Monica, California, United States
  • Atd002 52013 Boca Raton, Florida, United States
  • Atd002 52007 Miami, Florida, United States
View all 68 locations
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