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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,241 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Recruiting

A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

NCT06817382

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • USA012 Little Rock, Arkansas, United States
  • USA010 Davis, California, United States
  • USA009 Los Angeles, California, United States
  • USA002 Palo Alto, California, United States
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Recruiting

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

NCT07674758

Conditions
Becker Muscular Dystrophy, Cardiomyopathies, Cardiomyopathy, +14 more
Locations
  • UC Davis Sacramento, California, United States
  • Children's National Washington D.C., District of Columbia, United States
  • Lurie Children's Chicago, Illinois, United States
  • Riley Children's Hospital Indianapolis, Indiana, United States
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Recruiting

Study of MRM-3379 in Male Participants With Fragile X Syndrome (BLOOM)

NCT07209462

Conditions
Chromosome Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
Locations
  • Southwest Autism Research & Resource Center Phoenix, Arizona, United States
  • Amnova Clinical Research, LLC Irvine, California, United States
  • Children's Hospital of Orange County - Pediatric Subspecialty Orange, California, United States
  • Uc Davis Mind Institute Sacramento, California, United States
View all 15 locations
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Recruiting

Efficacy and Safety of CSL222 (Etranacogene Dezaparvovec) Gene Therapy in Adults With Hemophilia B With Pretreatment Adeno-associated Virus Serotype 5 (AAV5) Neutralizing Antibodies (Nabs)

NCT06003387

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • University of California, San Diego (UCSD) San Diego, California, United States
  • University of Michigan Ann Arbor, Michigan, United States
  • Hemophilia Center of Western Pennsylvania (HCWP) Pittsburgh, Pennsylvania, United States
  • Royal Prince Alfred Hospital Camperdown, New South Wales, Australia
View all 30 locations
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Recruiting

Danon Disease Natural History Study

NCT06214507

Conditions
Carbohydrate Metabolism, Inborn Errors, Cardiomyopathies, Cardiovascular Diseases, +15 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • University of California, San Diego La Jolla, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • University of Florida College of Medicine Gainesville, Florida, United States
View all 15 locations
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Recruiting

Sertraline vs. Placebo in the Treatment of Anxiety in Children and AdoLescents With NeurodevelopMental Disorders

NCT06081348

Conditions
22Q11 Deletion, 22q11 Deletion Syndrome, ADHD, +59 more
Locations
  • Alberta Children's Hospital - University of Calgary Calgary, Alberta, Canada
  • University of Alberta-Glenrose Edmonton, Alberta, Canada
  • Dalhousie University - IWK Health Centre Halifax, Nova Scotia, Canada
  • McMaster University Hamilton, Ontario, Canada
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