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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,249 public trials 232 recruiting studies
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Genetic Diseases, X-Linked trial results

Recruiting

The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy

NCT07092540

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
Locations
  • University of Rochester Rochester, New York, United States
  • Stony Brook Medicine Stony Brook, New York, United States
  • Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
  • Nationwide Children's Hospital Columbus, Ohio, United States
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Recruiting

A Study to Compare the Efficacy and Safety of BMS-986365 Versus the Investigator's Choice of Therapy in Participants With Metastatic Castration-resistant Prostate Cancer

NCT06764485

Conditions
Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +20 more
Locations
  • Central Alabama Research Birmingham, Alabama, United States
  • Banner MD Anderson Cancer Center Gilbert, Arizona, United States
  • Local Institution - 0370 Anaheim, California, United States
  • Moores Cancer Center La Jolla, California, United States
View all 281 locations
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Recruiting

A Phase 3 Study of Fenfluramine Hydrochloride in Rett Syndrome

NCT07503444

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • Ep0247 21010 Little Rock, Arkansas, United States
  • Ep0247 21011 Orlando, Florida, United States
  • Ep0247 21005 Houston, Texas, United States
  • Ep0247 21013 Irving, Texas, United States
View all 18 locations
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Recruiting

A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping

NCT07587242

Conditions
Congenital, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, +22 more
Locations
  • AP-HP Hospital Armand-Trousseau Paris, France
  • Universitaetsklinikum Essen Essen, Germany
  • Universitaetsklinikum Heidelberg Heidelberg, Germany
  • Klinikum der Ludwig-Maximilians-Universitaet Muenchen München, Germany
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Recruiting

ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

NCT04398628

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +34 more
Locations
  • Arizona Hemophilia and Thrombosis Treatment Center at Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Center for Bleeding Disorders Little Rock, Arkansas, United States
  • Orthopaedic Institute for Children HTC Los Angeles, California, United States
  • Childrens Hospital Los Angeles Los Angeles, California, United States
View all 76 locations
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Recruiting

Prevalence of Antibodies and Cytokines in Participants With Chronic Granulomatous Disease

NCT06605378

Conditions
Chronic Disease, Chronic Granulomatous Disease (CGD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
Locations
  • Home-based telemedicine Montgomery, Alabama, United States
  • Home-based telemedicine Phoenix, Arizona, United States
  • Home-based telemedicine Little Rock, Arkansas, United States
  • Home-based telemedicine Sacramento, California, United States
View all 52 locations
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