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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,242 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Recruiting

Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy

NCT05933057

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Universitaire Ziekenhuizen Leuven Leuven, Belgium
  • British Columbia Children's Hospital Vancouver, British Columbia, Canada
  • The University of Western Ontario - Children's Health Research Institute London, Ontario, Canada
  • University of Ottawa - Children's Hospital of Eastern Ontario Ottawa, Ontario, Canada
View all 29 locations
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Recruiting

A Study to Learn About the Investigational Drug Rinzimetostat (ORIC-944) in Patients With mCRPC Who Were Previously Treated With Abiraterone Acetate (Himalayas-1)

NCT07723248

Conditions
Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +24 more
Locations
  • Urology Specialists of the Carolinas - University Place Charlotte, North Carolina, United States
  • Summit Urology Murray, Utah, United States
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Recruiting

A Study to Compare the Efficacy and Safety of BMS-986365 Versus the Investigator's Choice of Therapy in Participants With Metastatic Castration-resistant Prostate Cancer

NCT06764485

Conditions
Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +20 more
Locations
  • Central Alabama Research Birmingham, Alabama, United States
  • Banner MD Anderson Cancer Center Gilbert, Arizona, United States
  • Local Institution - 0370 Anaheim, California, United States
  • Moores Cancer Center La Jolla, California, United States
View all 281 locations
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Recruiting

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

NCT07287189

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +10 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Colorado Children's Aurora, Colorado, United States
  • Lurie Children's Chicago, Illinois, United States
  • UMass Memorial Medical Center Worcester, Massachusetts, United States
View all 21 locations
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Recruiting

Phase 3, Open-label, Single-dose Study of CSL222 in Adolescent Male Subjects (≥ 12 to < 18 Years of Age) With Severe or Moderately Severe Hemophilia B

NCT07080905

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Center for Inherited Blood Disorders Orange, California, United States
  • University of Florida Gainesville, Florida, United States
  • Arthur M. Blank Hospital - Children's Healthcare of Atlanta Atlanta, Georgia, United States
  • University of Michigan Medical Center Ann Arbor, Michigan, United States
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Recruiting

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

NCT06564974

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Childrens Hospital Little Rock, Arkansas, United States
  • Loma Linda University Pediatric Subspecialty Clinics Loma Linda, California, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
View all 33 locations
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Recruiting

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

NCT07160634

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Neurology Rare Disease Center Flower Mound, Texas, United States
  • Children's Hospital of the King's Daughters Norfolk, Virginia, United States
  • The Children's Hospital of Westmead Sydney, New South Wales, Australia
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