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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,242 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Active, Not Recruiting

Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product

NCT02698579

Conditions
Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +24 more
Locations
  • Mattel Children's Hospital-UCLA Los Angeles, California, United States
  • Lucile Packard Children's Hospital - Stanford Palo Alto, California, United States
  • Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
  • University of Minnesota Minneapolis, Minnesota, United States
View all 13 locations
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Active, Not Recruiting

CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome)

NCT03566043

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
Locations
  • University of California San Francisco, Benioff Children's Hospital Oakland, California, United States
  • St. Peter's University Hospital New Brunswick, New Jersey, United States
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders Pittsburgh, Pennsylvania, United States
View Trial Details
Active, Not Recruiting

Observatory of Patients With Haemophilia B Treated by IdElvion®

NCT05086575

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
Locations
  • CHU Amiens - Picardie Amiens, France
  • CH Annecy Genevois Annecy, France
  • CHRU Besançon Besançon, France
  • CHU Bordeaux - Hôpital Pellegrin Bordeaux, France
View all 28 locations
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Active, Not Recruiting

Long Term Follow-up (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

NCT04628871

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Carbohydrate Metabolism, Inborn Errors, +24 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • New York University Grossman School of Medicine New York, United States
  • University of North Carolina Chapel Hill, North Carolina, United States
View Trial Details
Active, Not Recruiting

An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry Disease

NCT04519749

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of California at San Diego La Jolla, California, United States
  • Emory University Atlanta, Georgia, United States
  • Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
  • Lysosomal & Rare Disorders Research & Treatment Center, Inc Fairfax, Virginia, United States
View Trial Details

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