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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,242 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Active, Not Recruiting

Evaluation of the Safety and Efficacy of Hemophilia B Gene Therapy Drug

NCT05203679

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Anhui Provincial Hospital Hefei, Anhui, China
  • Peking Union Medical College Hospital Beijing, Beijing Municipality, China
  • Nanfang Hospital Southern Medical University Guangzhou, Guangdong, China
  • The Second People's Hospital of Shenzhen Shenzhen, Guangdong, China
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Active, Not Recruiting

Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita

NCT01659606

Conditions
Anemia, Anemia, Aplastic, Aplastic Anemia, +18 more
Locations
  • University of Chicago Chicago, Illinois, United States
  • Massachusetts General Hospital Boston, Massachusetts, United States
  • Boston Children's Hospital (pediatric patients) Boston, Massachusetts, United States
  • Dana-Farber Cancer Institute (adult patients) Boston, Massachusetts, United States
View all 13 locations
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Active, Not Recruiting

Open-Label Single Ascending Dose of Adeno-associated Virus Serotype 8 Factor IX Gene Therapy in Adults With Hemophilia B

NCT01687608

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Orthopaedic Hemophilia Treatment Center Los Angeles, California, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • University of California Davis Medical Center Sacramento, California, United States
  • University of California at San Diego Medical Center San Diego, California, United States
View all 15 locations
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Active, Not Recruiting

A Trial That Evaluates Disease Characteristics in Hemophilia B Adult Male Participants Receiving Prophylaxis With Standard of Care Factor IX Protein (FIX) Replacement Therapy

NCT05568459

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • University of Colorado Hemophilia and Thrombosis Center Aurora, Colorado, United States
  • Yale HTC New Haven, Connecticut, United States
  • Georgetown University Medical Center Washington D.C., District of Columbia, United States
  • University of Florida Gainesville, Florida, United States
View all 17 locations
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Active, Not Recruiting

International SBMA Project (KDA)

NCT07443449

Conditions
Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +11 more
Locations
  • Fondazione IRCCS Istituto Neurologico Carlo Besta Milan, Italy
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