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Clinical trial condition

Muscular Dystrophies

Explore clinical trials studying Muscular Dystrophies. Study availability and eligibility vary by location and protocol.

454 public trials 90 recruiting studies
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Muscular Dystrophies trial results

Recruiting

The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy

NCT07092540

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
Locations
  • University of Rochester Rochester, New York, United States
  • Stony Brook Medicine Stony Brook, New York, United States
  • Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
  • Nationwide Children's Hospital Columbus, Ohio, United States
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Recruiting

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

NCT07486934

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +18 more
Locations
  • UCSD - Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • IU Health Neuroscience Center Indianapolis, Indiana, United States
  • Roy Blunt NextGen Precision Health Institute Columbia, Missouri, United States
View all 34 locations
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Recruiting

A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45

NCT07038824

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
Locations
  • University Hospital Gent Ghent, Belgium
  • UZ Leuven Leuven, Belgium
  • Centre Hospitalier Régional de la Citadelle Liège, Belgium
  • IRCCS Ospedale San Raffaele Milan, Italy
View all 15 locations
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Recruiting

A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44

NCT07037862

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
Locations
  • University Hospital Gent Ghent, Belgium
  • UZ Leuven Leuven, Belgium
  • Centre Hospitalier Régional de la Citadelle Liège, Belgium
  • IRCCS Ospedale San Raffaele Milan, Italy
View all 14 locations
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Recruiting

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

NCT07160634

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Neurology Rare Disease Center Flower Mound, Texas, United States
  • Children's Hospital of the King's Daughters Norfolk, Virginia, United States
  • The Children's Hospital of Westmead Sydney, New South Wales, Australia
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Recruiting

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

NCT06747884

Conditions
Childhood Myotonic Dystrophy, Congenital Myotonic Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +16 more
Locations
  • Virginia Commonwealth University Richmond, Virginia, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
  • Hospital das Clínicas, University of São Paulo School of Medicine (HCFMUSP) Cerqueira César, São Paulo, Brazil
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Recruiting

Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular Dystrophy Type 1

NCT06131983

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Muscular Diseases, +6 more
Locations
  • Liverpool Hospital Liverpool, New South Wales, Australia
  • Wesley Research Institute Auchenflower, Queensland, Australia
  • Sunshine Coast University Hospital Birtinya, Queensland, Australia
  • Alfred Health Melbourne, Victoria, Australia
View all 16 locations
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Recruiting

Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy

NCT06138743

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
Locations
  • Liverpool Hospital Liverpool, New South Wales, Australia
  • Sunshine Coast University Hospital Birtinya, Queensland, Australia
  • Royal Brisbane And Women's Hospital Herston, Queensland, Australia
  • Alfred Health Melbourne, Victoria, Australia
View all 35 locations
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Recruiting

A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

NCT06817382

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • USA012 Little Rock, Arkansas, United States
  • USA010 Davis, California, United States
  • USA009 Los Angeles, California, United States
  • USA002 Palo Alto, California, United States
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