NCT03947112
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Haukeland University Hospital Bergen, Hordaland, Norway
Clinical trial condition
Genetic Diseases, X-Linked
Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.
1,244 public trials
227 recruiting studies
Genetic Diseases, X-Linked trial results
NCT03963453
- Conditions
- Behavior, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
-
- Department of Physiotherapy. Haukeland University Hospital Bergen, Norway
Completed
Gene Therapy for Chinese Hemophilia B
NCT04135300
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
- Locations
-
- Institute of Hematology & Blood Diseases Hospital Tianjin, Tianjin Municipality, China
NCT06257901
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Brunel University London London, United Kingdom
NCT04073498
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
- Locations
-
- Arensia Clinical Research Unit Tbilisi, Georgia
- Arensia Clinical Research Unit Chisinau, Moldova
- Simbec Research Ltd Merthyr Tydfil, Cardiff, United Kingdom
NCT06801288
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- IRCCS Sant'Orsola University Hospital - Nephrology, Dialysis and Transplant Unit Bologna, BO, Italy
NCT04571970
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- University of California San Francisco, Benioff Children's Hospital Oakland, California, United States
- McGill University Heath Center Montreal, Quebec, Canada
Completed
A Study of Elaprase in Children and Adults With Hunter Syndrome (Mucopolysaccharidosis II) in India
NCT05058391
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- SAT Hospital - Govt Medical College Thiruvananthapuram, Kerala, India
- JK Lone Hospital Jaipur, Rajasthan, India
- Institute of Child Health Kolkata, India
- All India Institute of Medical Sciences (AIIMS) New Delhi, India
NCT02485938
- Conditions
- Cardiomyopathies, Cardiomyopathy, Cardiovascular Diseases, +12 more
- Locations
-
- Cedars-Sinai Medical Center Los Angeles, California, United States
- University of Florida Gainesville, Florida, United States
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
NCT01999075
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Alberta Children's Hospital Calgary, Alberta, Canada
- Stollery Children's Hospital Edmonton, Alberta, Canada
- BC Children's Hospital Vancouver, British Columbia, Canada
- McMaster University Hamilton, Ontario, Canada