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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,243 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Recruiting

Biomarker Development for Muscular Dystrophies

NCT05019625

Conditions
Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, +15 more
Locations
  • Boston Children's Hospital Boston, Massachusetts, United States
  • Brigham and Women's Hospital Boston, Massachusetts, United States
  • Massachusetts General Hospital Boston, Massachusetts, United States
  • Wake Forest University Winston-Salem, North Carolina, United States
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Recruiting

An Open-Label, Comparative Study of the Efficacy, Safety and Pharmacodynamics of Single Dose of ANB-002 in Patients With Hemophilia B

NCT06700096

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Chelyabinsk Regional Clinical Hospital Chelyabinsk, Russia
  • Federal State Budgetary Organization of Science "Kirov Research Institute of Hematology and Blood Transfusions of Federal Medical Biological agency" Kirov, Russia
  • Federal State Budgetary Institution "National Medical Research Centre for Hematology" of the Ministry of Health of Russian Federation (Department of Clinical Diagnostics for Hematology and Hemostasis Disorders) Moscow, Russia
  • Federal State Budgetary Institution "National Medical Research Centre for Hematology" of the Ministry of Health of Russian Federation (Department of Traumatology and Reconstructive and Restorative Orthopedics for Patients with Hemophilia) Moscow, Russia
View all 14 locations
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Recruiting

A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

NCT06663358

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • Emory University School of Medicine Atlanta, Georgia, United States
  • Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of Iowa Hospitals and Clinics Iowa City, Iowa, United States
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Recruiting

The Myelin Disorders Biorepository Project

NCT03047369

Conditions
4H Syndrome, ADLD, AGS, +173 more
Locations
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Stanford University (Lucile Packard Children's Hospital) Palo Alto, California, United States
  • University of California, Davis (UC Davis Health) Sacramento, California, United States
View all 23 locations
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Recruiting

Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease

NCT06270316

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • The Kirklin Clinic Of university of Alabama Birmingham Hospital Birmingham, Alabama, United States
  • Emory University School of Medicine Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • MHealth Fairview University of Minnesota Medical Center East Bank Minneapolis, Minnesota, United States
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