Enrolling by invitation
A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice
NCT06606340
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Arkansas Children's Hospital Research Institute Little Rock, Arkansas, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
- University of California Davis Medical Center Sacramento, California, United States
- Children's National Hospital Washington D.C., District of Columbia, United States