Enrolling by Invitation
Long Term Follow-up for RGX-202
NCT06491927
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Stanford School of Medicine /Division of Neuromuscular Medicine Palo Alto, California, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- The University of Texas Southwestern Medical Center Dallas, Texas, United States