Active, Not Recruiting
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)
NCT05881408
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Lucile Packard Children's Hospital Stanford Palo Alto, California, United States
- University of California at Davis Medical Center Sacramento, California, United States
- Rady Children's Hospital-San Diego San Diego, California, United States