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Clinical trial condition

Duchenne Muscular Dystrophy

Explore clinical trials studying Duchenne Muscular Dystrophy. Study availability and eligibility vary by location and protocol.

214 public trials 28 recruiting studies
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Duchenne Muscular Dystrophy trial results

Active, Not Recruiting

Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping

NCT06244082

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +11 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • University of California, San Diego, Rady's Children's Hospital La Jolla, California, United States
  • UC Davis Medical Center Sacramento, California, United States
  • Lucille Packard Children's Hospital at Stanford San Carlos, California, United States
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Active, Not Recruiting

Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy

NCT04281485

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Arkansas Children's Little Rock, Arkansas, United States
  • UCLA Medical Center Los Angeles, California, United States
  • University of Florida Gainesville, Florida, United States
View all 53 locations
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Active, Not Recruiting

AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)

NCT05693142

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Stanford School of Medicine /Division of Neuromuscular Medicine Palo Alto, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
View all 23 locations
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Active, Not Recruiting

Early Check: Expanded Screening in Newborns

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States
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Active, Not Recruiting

A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy

NCT06280209

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Fondazione Serena ETS - Centro Clinico NeMO Milano Milan, Italy
  • UOC Fase I - Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore Rome, Italy
  • Leids Universitair Medisch Centrum Leiden, Netherlands
  • Hospital Sant Joan de Deu Barcelona, Spain
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Active, Not Recruiting

NS-050/NCNP-03 in Boys With DMD (Meteor50)

NCT06053814

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
View all 19 locations
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