NCT02251600
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- UCLA Los Angeles, California, United States
- Lurie Children's Hospital Chicago, Illinois, United States
- University of Rochester Medical Center Rochester, New York, United States
- University of Utah Salt Lake City, Utah, United States