- Conditions
- Atrophy, Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, +19 more
- Locations
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- Boston Childrens Hospital Boston, Massachusetts, United States
- Child Hosp Of The Kings Daughters Norfolk, Virginia, United States
- University of Wisconsin Madison Medical School Madison, Wisconsin, United States
- Novartis Investigative Site Parkville, Victoria, Australia
Clinical trial condition
Spinal Muscular Atrophy
Explore clinical trials studying Spinal Muscular Atrophy. Study availability and eligibility vary by location and protocol.
111 public trials
17 recruiting studies
Spinal Muscular Atrophy trial results
NCT00961103
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- UDGEE Hospital S.Maria Nuova Reggio Emilia, RE, Italy
NCT04773470
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- University Hospital Giessen and Marburg, Campus Giessen Giessen, Hesse, Germany
Completed
Mechanisms and Treatment of Exercise Intolerance and Persistent Fatigue in Spinal Muscular Atrophy
NCT05518773
- Conditions
- Behavior, Central Nervous System Diseases, Fatigue, +10 more
- Locations
-
- Columbia University Irving Medical Center New York, United States
NCT02386553
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- David Geffen School of Medicine Los Angeles, California, United States
- University of California Davis Health System Sacramento, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Nemours Children's Hospital, Orlando Orlando, Florida, United States
Completed
A Study of Risdiplam (RO7034067) in Adult and Pediatric Participants With Spinal Muscular Atrophy
NCT03032172
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- Stanford University Medical Center Palo Alto, California, United States
- Nemours Children's Hospital Orlando, Florida, United States
- Boston Childrens Hospital Boston, Massachusetts, United States
- Columbia University Medical Center New York, United States
NCT05712330
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +7 more
- Locations
-
- Centre Hospitalier Universitaire d'Amiens Amiens, Picardie, France
NCT02268552
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- Novartis Investigative Site Ghent, Belgium
- Novartis Investigative Site Leuven, Belgium
- Novartis Investigative Site Sofia, Bulgaria
- Novartis Investigative Site Copenhagen, Denmark
NCT00227266
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- Johns Hopkins University Baltimore, Maryland, United States
- Children's Hospital of Michigan Detroit, Michigan, United States
- Ohio State University Columbus, Ohio, United States
- University of Utah/Primary Children's Medical Center Salt Lake City, Utah, United States
NCT05366465
- Conditions
- Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
- Locations
-
- Service L'Escale - Médecine Physique et de Réadaptation Pédiatrique Groupement Hospitalier Est des Hospices Civils de Lyon Bron, France
- VUILLEROT Carole Bron, France