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Clinical trial condition

Spinal Muscular Atrophy

Explore clinical trials studying Spinal Muscular Atrophy. Study availability and eligibility vary by location and protocol.

113 public trials 20 recruiting studies
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Spinal Muscular Atrophy trial results

Completed

A Study of Multiple Doses of Nusinersen (ISIS 396443) Delivered to Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy

NCT02386553

Conditions
Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations
  • David Geffen School of Medicine Los Angeles, California, United States
  • University of California Davis Health System Sacramento, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Nemours Children's Hospital, Orlando Orlando, Florida, United States
View all 21 locations
View Trial Details
Completed

A Study of Risdiplam (RO7034067) in Adult and Pediatric Participants With Spinal Muscular Atrophy

NCT03032172

Conditions
Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations
  • Stanford University Medical Center Palo Alto, California, United States
  • Nemours Children's Hospital Orlando, Florida, United States
  • Boston Childrens Hospital Boston, Massachusetts, United States
  • Columbia University Medical Center New York, United States
View all 24 locations
View Trial Details
Completed

An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA)

NCT02268552

Conditions
Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations
  • Novartis Investigative Site Ghent, Belgium
  • Novartis Investigative Site Leuven, Belgium
  • Novartis Investigative Site Sofia, Bulgaria
  • Novartis Investigative Site Copenhagen, Denmark
View all 14 locations
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Completed

Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy

NCT00227266

Conditions
Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations
  • Johns Hopkins University Baltimore, Maryland, United States
  • Children's Hospital of Michigan Detroit, Michigan, United States
  • Ohio State University Columbus, Ohio, United States
  • University of Utah/Primary Children's Medical Center Salt Lake City, Utah, United States
View Trial Details
Completed

Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases

NCT02532244

Conditions
Amyotrophic Lateral Sclerosis, Central Nervous System Diseases, Charcot-Marie-Tooth Disease, +28 more
Locations
  • Nemours Children's Hospital Delaware Wilmington, Delaware, United States
  • Nemours Children's Specialty Care Jacksonville, Florida, United States
  • Nemours Children's Hospital Orlando Orlando, Florida, United States
View Trial Details

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