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Clinical trial condition

Spinal Muscular Atrophy

Explore clinical trials studying Spinal Muscular Atrophy. Study availability and eligibility vary by location and protocol.

111 public trials 17 recruiting studies

Spinal Muscular Atrophy trial results

Conditions
Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • Stanford Neuroscience Health Center Palo Alto, California, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
View all 22 locations
Conditions
Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations
  • CHU de Lyon Lyon, Auvergne-Rhône-Alpes, France
  • CHRU de Lille Lille, Hauts-de-France, France
  • CHU de Montpellier Montpellier, Occitanie, France
  • CHU de Toulouse Toulouse, Occitanie, France
Conditions
Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
Locations
  • Phoenix Childrens Hospital Phoenix, Arizona, United States
  • UCSD Altman Clinical and Translational Research La Jolla, California, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • Stanford Neuroscience Health Center Palo Alto, California, United States
View all 49 locations

NCT03709784

Conditions
Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • Georgetown University Washington D.C., District of Columbia, United States
  • Johns Hopkins Baltimore, Maryland, United States
  • Massachusetts General Hospital-Harvard University Boston, Massachusetts, United States