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Clinical trial condition

Spinal Muscular Atrophy

Explore clinical trials studying Spinal Muscular Atrophy. Study availability and eligibility vary by location and protocol.

111 public trials 17 recruiting studies
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Spinal Muscular Atrophy trial results

Completed

Optimum Insufflation Capacity in NMD

NCT01981915

Conditions
Central Nervous System Diseases, Chronic Respiratory Insufficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +15 more
Locations
  • University of Essen, Children's Hospital, Dep. of Pediatric Pulmonology Essen, North Rhine-Westphalia, Germany
View Trial Details
Completed

A Pilot Study of Biomarkers for Spinal Muscular Atrophy

NCT00756821

Conditions
Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • Stanford University Stanford, California, United States
  • The Children's Hospital Aurora, Colorado, United States
  • University of Iowa Iowa City, Iowa, United States
View all 18 locations
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Active, Not Recruiting

Long-term Follow-up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA)

NCT05232929

Conditions
Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • University of Arkansas for Medical Sciences Little Rock, Arkansas, United States
  • Loma Linda University Health Care Loma Linda, California, United States
View all 38 locations
View Trial Details
Active, Not Recruiting

Early Check: Expanded Screening in Newborns

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States
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Active, Not Recruiting

A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy

NCT05337553

Conditions
Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +6 more
Locations
  • Phoenix Children's Phoenix, Arizona, United States
  • UCSD & Rady Children's La Jolla, California, United States
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • UCSF Benioff Children's Hospital, Medical Center San Francisco, California, United States
View all 53 locations
View Trial Details

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