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Spinal Muscular Atrophy

Clinical trial condition

Spinal Muscular Atrophy

Explore clinical trials studying Spinal Muscular Atrophy. Study availability and eligibility vary by location and protocol.

113 public trials 20 recruiting studies

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Spinal Muscular Atrophy trial results

Not yet recruiting

A Study of the Safety and Effectiveness of Onasemnogene Abeparvovec (Zolgensma) Intrathecal Injection in Spinal Muscular Atrophy Patients

NCT07767890

Conditions: Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations: Not specified

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Not yet recruiting

Spinal Muscular Atrophy and School Transitions

NCT07720518

Conditions: Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations: The Robert Jones & Agnes Hunt Orthopaedic Hospital Oswestry, Shropshire, United Kingdom

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Enrolling by invitation

Development and Validation of the FBIndex to Determine the Risk of Falls for Patients With Neuromuscular Disorders

NCT06605612

Conditions: Amyotrophic Lateral Sclerosis, Autoimmune Diseases, Autoimmune Diseases of the Nervous System, +67 more
Locations: Friedrich-Baur-Institut, Neurologische Klinik und Poliklinik, LMU Klinikum, Ludwig-Maximilians-Universität München München, Bavaria, Germany

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Enrolling by invitation

A Long-term Follow-up Study Evaluating Intravenous Injection of EXG001-307 in Patients With Type 1 SMA

NCT06588803

Conditions: Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations: The Children's Hospital of Fudan University Shanghai, Shanghai Municipality, China

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Active, not recruiting

Long-term Follow-up Study of Risdiplam in Participants With Spinal Muscular Atrophy (SMA)

NCT05232929

Conditions: Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations: Barrow Neurological Institute Phoenix, Arizona, United States

Phoenix Children's Hospital Phoenix, Arizona, United States

University of Arkansas for Medical Sciences Little Rock, Arkansas, United States

Loma Linda University Health Care Loma Linda, California, United States

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Active, not recruiting

COMMAND Early Feasibility Study: Implantable BCI to Control a Digital Device for People With Paralysis

NCT05035823

Conditions: Amyotrophic Lateral Sclerosis, Brain Diseases, Brain Infarction, +46 more
Locations: University at Buffalo Neurosurgery (UBNS) Buffalo, New York, United States

Mount Sinai Health System New York, United States

University of Pittsburgh Medical Center Pittsburgh, Pennsylvania, United States

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Active, not recruiting

Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab

NCT05626855

Conditions: Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
Locations: Phoenix Childrens Hospital Phoenix, Arizona, United States

UCSD Altman Clinical and Translational Research La Jolla, California, United States

Children's Hospital Los Angeles Los Angeles, California, United States

Stanford Neuroscience Health Center Palo Alto, California, United States

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Active, not recruiting

Early Check: Expanded Screening in Newborns

NCT03655223

Conditions: 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations: RTI International Research Triangle Park, North Carolina, United States

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Active, not recruiting

An Open Label Study of Gene Therapy Product (Vesemnogene Lantuparvovec) in Spinal Muscular Atrophy

NCT06288230

Conditions: Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +5 more
Locations: Kunming Hope of Health Hospital Kunming, Yunnan, China

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Active, not recruiting

A Study to Evaluate the Efficacy and Safety of Taldefgrobep Alfa in Participants With Spinal Muscular Atrophy

NCT05337553

Conditions: Central Nervous System Diseases, Motor Neuron Disease, Muscular Atrophy, Spinal, +6 more
Locations: Phoenix Children's Phoenix, Arizona, United States

UCSD & Rady Children's La Jolla, California, United States

Children's Hospital of Los Angeles Los Angeles, California, United States

UCSF Benioff Children's Hospital, Medical Center San Francisco, California, United States

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Spinal Muscular Atrophy

Spinal Muscular Atrophy trial results

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