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Clinical trial condition

Muscular Dystrophy, Duchenne

Explore clinical trials studying Muscular Dystrophy, Duchenne. Study availability and eligibility vary by location and protocol.

357 public trials 57 recruiting studies
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Muscular Dystrophy, Duchenne trial results

Active, Not Recruiting

Early Check: Expanded Screening in Newborns

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States
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Active, Not Recruiting

A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy

NCT06280209

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Fondazione Serena ETS - Centro Clinico NeMO Milano Milan, Italy
  • UOC Fase I - Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore Rome, Italy
  • Leids Universitair Medisch Centrum Leiden, Netherlands
  • Hospital Sant Joan de Deu Barcelona, Spain
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Active, Not Recruiting

NS-050/NCNP-03 in Boys With DMD (Meteor50)

NCT06053814

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
View all 19 locations
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Active, Not Recruiting

Defining Endpoints in Becker Muscular Dystrophy

NCT05257473

Conditions
Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
Locations
  • University of California, Irvine Orange, California, United States
  • University of Colorado Anschutz Medical Campus Aurora, Colorado, United States
  • University of Iowa Iowa City, Iowa, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
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Active, Not Recruiting

A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy

NCT05126758

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • UCSD Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Children's Hospital of Los Angeles, Division of Neurology Los Angeles, California, United States
View all 20 locations
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Active, Not Recruiting

A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)

NCT05881408

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Lucile Packard Children's Hospital Stanford Palo Alto, California, United States
  • University of California at Davis Medical Center Sacramento, California, United States
  • Rady Children's Hospital-San Diego San Diego, California, United States
View all 46 locations
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Active, Not Recruiting

Phase 2 Study of EDG-5506 in Becker Muscular Dystrophy (GRAND CANYON)

NCT05291091

Conditions
Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • UC San Diego La Jolla, California, United States
  • UCLA Medical Center Los Angeles, California, United States
  • UC Irvine Medical Center Orange, California, United States
View all 51 locations
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Active, Not Recruiting

A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD)

NCT06450639

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Fractures, Bone, +13 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • University of California Davis Medical Center Sacramento, California, United States
  • Children's Healthcare of Atlanta Center for Advanced Pediatrics Atlanta, Georgia, United States
  • Corewell Health Grand Rapids, Michigan, United States
View all 19 locations
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Active, Not Recruiting

A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)

NCT06128564

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Chr de La Citadelle Liège, Belgium
  • Hôpital Necker-Enfants Malades Paris, France
  • Universitätsklinikum Essen Essen, Germany
  • PU A. Gemelli, Università Cattolica del Sacro Cuore Rome, Lazio, Italy
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