Recruiting
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
NCT07160634
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Neurology Rare Disease Center Flower Mound, Texas, United States
- Children's Hospital of the King's Daughters Norfolk, Virginia, United States
- The Children's Hospital of Westmead Sydney, New South Wales, Australia