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Clinical trial condition

Muscular Dystrophy, Duchenne

Explore clinical trials studying Muscular Dystrophy, Duchenne. Study availability and eligibility vary by location and protocol.

362 public trials 56 recruiting studies
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Muscular Dystrophy, Duchenne trial results

Active, not recruiting

A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)

NCT06128564

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Chr de La Citadelle Liège, Belgium
  • Hôpital Necker-Enfants Malades Paris, France
  • Universitätsklinikum Essen Essen, Germany
  • PU A. Gemelli, Università Cattolica del Sacro Cuore Rome, Lazio, Italy
View Trial Details
Active, not recruiting

A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD)

NCT06450639

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Fractures, Bone, +13 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • University of California Davis Medical Center Sacramento, California, United States
  • Children's Healthcare of Atlanta Center for Advanced Pediatrics Atlanta, Georgia, United States
  • Corewell Health Grand Rapids, Michigan, United States
View all 18 locations
View Trial Details
Active, not recruiting

Defining Endpoints in Becker Muscular Dystrophy

NCT05257473

Conditions
Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
Locations
  • University of California, Irvine Orange, California, United States
  • University of Colorado Anschutz Medical Campus Aurora, Colorado, United States
  • University of Iowa Iowa City, Iowa, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
View Trial Details
Active, not recruiting

A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy

NCT05126758

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • UCSD Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Children's Hospital of Los Angeles, Division of Neurology Los Angeles, California, United States
View all 20 locations
View Trial Details
Active, not recruiting

Study of UC-MSC in DMD Patients

NCT06579352

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Other locations - TBD Dallas, Texas, United States
  • Neurology Rare Disease Center Flower Mound, Texas, United States
View Trial Details
Active, not recruiting

Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51 Skipping

NCT05524883

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
Locations
  • University of California San Diego La Jolla, California, United States
  • UCLA University California of Los Angeles Los Angeles, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
View all 30 locations
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Active, not recruiting

An Open-label, Multidose Dose-escalation Study to Understand the Safety of CRISPR Gene-editing Therapy and Its Long-Lasting Effects in DMD Patients (MUSCLE)

NCT06594094

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophin (DMD), Genetic Diseases, Inborn, +8 more
Locations
  • Shanghai Children s Medical Center Affiliated to Shanghai Jiao Tong University School of Medical Shanghai, Shanghai Municipality, China
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Active, not recruiting

Ph2 Open-label Study of AOC 1044 in Duchenne Muscular Dystrophy Participants With Mutations Amenable to Exon44 Skipping

NCT06244082

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +11 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • University of California, San Diego, Rady's Children's Hospital La Jolla, California, United States
  • UC Davis Medical Center Sacramento, California, United States
  • Lucille Packard Children's Hospital at Stanford San Carlos, California, United States
View Trial Details
Active, not recruiting

Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy

NCT04281485

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Arkansas Children's Little Rock, Arkansas, United States
  • UCLA Medical Center Los Angeles, California, United States
  • University of Florida Gainesville, Florida, United States
View all 53 locations
View Trial Details

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