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Clinical trial condition

Muscular Dystrophies

Explore clinical trials studying Muscular Dystrophies. Study availability and eligibility vary by location and protocol.

452 public trials 90 recruiting studies
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Muscular Dystrophies trial results

Active, Not Recruiting

A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4

NCT06246513

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb-girdle Muscular Dystrophy, +7 more
Locations
  • University of California, San Diego-Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Nationwide Childrens Hospital Columbus, Ohio, United States
  • The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Children's Hospital of The King's Daughter Norfolk, Virginia, United States
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Active, Not Recruiting

A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)

NCT03992430

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • University of Florida Gainesville, Florida, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • Hospital Universitario San Ignacio Bogotá, Colombia
View all 59 locations
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Active, Not Recruiting

A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)

NCT05876780

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb Girdle Muscular Dystrophy, +7 more
Locations
  • Nationwide Children's Hospital Columbus, Ohio, United States
  • St. Jude Children's Research Hospital Memphis, Tennessee, United States
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Active, Not Recruiting

Global Study of Del-desiran for the Treatment of DM1

NCT06411288

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +21 more
Locations
  • Stanford University Stanford, California, United States
  • University of Colorado Denver, Colorado, United States
  • University of Florida Gainesville, Florida, United States
  • University Research Center of South Florida Tampa, Florida, United States
View all 34 locations
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Active, Not Recruiting

A Study of EDG-5506 in Children With Duchenne Muscular Dystrophy (LYNX)

NCT05540860

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • UCLA Medical Center Los Angeles, California, United States
  • UC Davis Medical Center Sacramento, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
View all 14 locations
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Active, Not Recruiting

Phase 2 Study of EDG-5506 in Children and Adolescents With Duchenne Muscular Dystrophy Previously Treated With Gene Therapy

NCT06100887

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • UCLA Medical Center Los Angeles, California, United States
  • UC Davis Medical Center Sacramento, California, United States
  • University of Florida Gainesville, Florida, United States
  • University of Massachusetts Memorial Medical Center Worcester, Massachusetts, United States
View Trial Details

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