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Clinical trial condition

Muscular Dystrophies

Explore clinical trials studying Muscular Dystrophies. Study availability and eligibility vary by location and protocol.

452 public trials 90 recruiting studies
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Muscular Dystrophies trial results

Recruiting

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

NCT07486934

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +18 more
Locations
  • UCSD - Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • IU Health Neuroscience Center Indianapolis, Indiana, United States
  • Roy Blunt NextGen Precision Health Institute Columbia, Missouri, United States
View all 24 locations
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Recruiting

A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

NCT06817382

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • USA012 Little Rock, Arkansas, United States
  • USA010 Davis, California, United States
  • USA009 Los Angeles, California, United States
  • USA002 Palo Alto, California, United States
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Recruiting

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

NCT07674758

Conditions
Becker Muscular Dystrophy, Cardiomyopathies, Cardiomyopathy, +14 more
Locations
  • UC Davis Sacramento, California, United States
  • Children's National Washington D.C., District of Columbia, United States
  • Lurie Children's Chicago, Illinois, United States
  • Riley Children's Hospital Indianapolis, Indiana, United States
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Recruiting

A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD

NCT07038200

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FSH Muscular Dystrophy, FSHD, +25 more
Locations
  • University of California Irvine Orange, California, United States
  • Stanford University Palo Alto, California, United States
  • University of Colorado Denver, Colorado, United States
  • University of Florida Gainesville, Florida, United States
View all 46 locations
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Recruiting

Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy

NCT05933057

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Universitaire Ziekenhuizen Leuven Leuven, Belgium
  • British Columbia Children's Hospital Vancouver, British Columbia, Canada
  • The University of Western Ontario - Children's Health Research Institute London, Ontario, Canada
  • University of Ottawa - Children's Hospital of Eastern Ontario Ottawa, Ontario, Canada
View all 29 locations
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Recruiting

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

NCT07160634

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Neurology Rare Disease Center Flower Mound, Texas, United States
  • Children's Hospital of the King's Daughters Norfolk, Virginia, United States
  • The Children's Hospital of Westmead Sydney, New South Wales, Australia
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Recruiting

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

NCT06138639

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • University of California, Los Angeles Medical Center Los Angeles, California, United States
  • University of California, Davis Sacramento, California, United States
  • University of California San Diego, California, United States
View all 15 locations
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Recruiting

A Study to Evaluate the Tolerability, Safety and Efficacy of GNR-097 Gene Therapy in Pediatric Patients With Duchenne Muscular Dystrophy

NCT07673809

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Republican Scientific and Practical Center Mother and Child Minsk, Belarus
  • Russian Children's Clinical Hospital Moscow, Russia
  • National Medical Research Center for Children Moscow, Russia
  • Veltischev Research and Clinical Institute for Pediatrics and Pediatric Surgery of the Pirogov Russian National Research Medical University Moscow, Russia
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Recruiting

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

NCT04626674

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Stanford University Palo Alto, California, United States
  • University of California, Davis Sacramento, California, United States
  • Washington University in St. Louis St Louis, Missouri, United States
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