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Clinical trial condition

Muscular Dystrophies

Explore clinical trials studying Muscular Dystrophies. Study availability and eligibility vary by location and protocol.

452 public trials 90 recruiting studies

Muscular Dystrophies trial results

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), Genetic Diseases, Inborn, +8 more
Locations
  • Fondazione Serena ETS - Centro Clinico NeMO Milano Milan, Italy
  • UOC Fase I - Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore Rome, Italy
  • Leids Universitair Medisch Centrum Leiden, Netherlands
  • Hospital Viamed Santa Angela De la Cruz Seville, Spain
Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +19 more
Locations
  • University of California, Los Angeles (UCLA) Los Angeles, California, United States
  • Stanford University Stanford, California, United States
  • University of Colorado Denver, Colorado, United States
  • University of Florida Gainesville, Florida, United States
View all 35 locations
Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
Locations
  • Chinese People's Liberation Army General Hospital Beijing, Beijing Municipality, China
  • Peking University First Hospital Beijing, Beijing Municipality, China
  • First Affiliated Hospital of Chongqing Medical University Chongqing, Chongqing Municipality, China
  • Fujian Medical University Union Hospital Fuzhou, Fujian, China
View all 22 locations
Conditions
Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • UC San Diego La Jolla, California, United States
  • UCLA Medical Center Los Angeles, California, United States
  • UC Irvine Medical Center Orange, California, United States
View all 46 locations
Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Children's Hospital Los Angeles - PIN Los Angeles, California, United States
  • University of Colorado - PPDS Aurora, Colorado, United States
  • Connecticut Children's Medical Center - Hartford Hartford, Connecticut, United States
View all 25 locations
Enrolling by Invitation

Long Term Follow-up for RGX-202

NCT06491927

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Stanford School of Medicine /Division of Neuromuscular Medicine Palo Alto, California, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • The University of Texas Southwestern Medical Center Dallas, Texas, United States