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Clinical trial condition

Muscular Disorders, Atrophic

Explore clinical trials studying Muscular Disorders, Atrophic. Study availability and eligibility vary by location and protocol.

621 public trials 123 recruiting studies
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Muscular Disorders, Atrophic trial results

Active, Not Recruiting

Clinical Trial Readiness to Solve Barriers to Drug Development in FSHD

NCT03458832

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
  • Kennedy Krieger Institute Baltimore, Maryland, United States
  • University of Rochester Medical Center Rochester, New York, United States
View all 14 locations
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Active, Not Recruiting

A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4

NCT06246513

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb-girdle Muscular Dystrophy, +7 more
Locations
  • University of California, San Diego-Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Nationwide Childrens Hospital Columbus, Ohio, United States
  • The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Children's Hospital of The King's Daughter Norfolk, Virginia, United States
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Active, Not Recruiting

A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)

NCT03992430

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • University of Florida Gainesville, Florida, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • Hospital Universitario San Ignacio Bogotá, Colombia
View all 59 locations
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Active, Not Recruiting

A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)

NCT05876780

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb Girdle Muscular Dystrophy, +7 more
Locations
  • Nationwide Children's Hospital Columbus, Ohio, United States
  • St. Jude Children's Research Hospital Memphis, Tennessee, United States
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Active, Not Recruiting

Global Study of Del-desiran for the Treatment of DM1

NCT06411288

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +21 more
Locations
  • Stanford University Stanford, California, United States
  • University of Colorado Denver, Colorado, United States
  • University of Florida Gainesville, Florida, United States
  • University Research Center of South Florida Tampa, Florida, United States
View all 34 locations
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