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Clinical trial condition

Muscular Disorders, Atrophic

Explore clinical trials studying Muscular Disorders, Atrophic. Study availability and eligibility vary by location and protocol.

621 public trials 123 recruiting studies
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Muscular Disorders, Atrophic trial results

Active, Not Recruiting

AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)

NCT05693142

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Stanford School of Medicine /Division of Neuromuscular Medicine Palo Alto, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
View all 23 locations
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Active, Not Recruiting

A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy

NCT06907875

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
Locations
  • David Geffen School of Medicine at University of California, Los Angeles Los Angeles, California, United States
  • Rare Disease Research Atlanta, Georgia, United States
  • Kennedy Krieger Institute, Center for Genetic Muscle Disorders Baltimore, Maryland, United States
  • University of Massachusetts Chan Medical School Worcester, Massachusetts, United States
View Trial Details
Active, Not Recruiting

Phase 2 Open-label Extension Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD)

NCT06547216

Conditions
Atrophies, Facioscapulohumeral, Atrophy, Facioscapulohumeral, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +33 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Stanford University Palo Alto, California, United States
  • University of California San Diego San Diego, California, United States
  • University of Colorado Denver, Colorado, United States
View all 17 locations
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Active, Not Recruiting

Early Check: Expanded Screening in Newborns

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States
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Active, Not Recruiting

A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy

NCT06280209

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Fondazione Serena ETS - Centro Clinico NeMO Milano Milan, Italy
  • UOC Fase I - Fondazione Policlinico Universitario A. Gemelli IRCCS - Universita Cattolica del Sacro Cuore Rome, Italy
  • Leids Universitair Medisch Centrum Leiden, Netherlands
  • Hospital Sant Joan de Deu Barcelona, Spain
View Trial Details
Active, Not Recruiting

A Study to Evaluate RO7204239 in Participants With Facioscapulohumeral Muscular Dystrophy

NCT05548556

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy (FSHD), Genetic Diseases, Inborn, +7 more
Locations
  • University of Irvine Medical Center (UCIMC) Orange, California, United States
  • Regents of the University of Colorado Aurora, Colorado, United States
  • University of Kansas Medical Center Fairway, Kansas, United States
  • Kennedy Krieger Institute Baltimore, Maryland, United States
View Trial Details
Active, Not Recruiting

NS-050/NCNP-03 in Boys With DMD (Meteor50)

NCT06053814

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
View all 19 locations
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