Completed
Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
NCT02369731
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
- Locations
-
- Krankenhaus der Barmherzigen Schwestern Linz Linz, Austria
- Sozialmedizinisches Zentrum Süd Kaiser-Franz-Josef Spital mit Gottfried von Preyer´schen Kinderspital Vienna, Austria
- Hospital das Clínicas da Universidade de São Paulo São Paulo, Brazil
- The University Hospital Brno Brno, Czechia