Enrolling by Invitation
An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy
NCT06270719
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
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- Arkansas Children's Hospital Little Rock, Arkansas, United States
- Children's Hospital Los Angeles - PIN Los Angeles, California, United States
- University of Colorado - PPDS Aurora, Colorado, United States
- Connecticut Children's Medical Center - Hartford Hartford, Connecticut, United States