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OpenTrials

Clinical trial condition

Mucopolysaccharidosis I

Explore clinical trials studying Mucopolysaccharidosis I. Study availability and eligibility vary by location and protocol.

53 public trials 6 recruiting studies
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Mucopolysaccharidosis I trial results

Completed

A Study Evaluating the Safety and Pharmacokinetics of Aldurazyme® (Laronidase) in MPS I Patients Less Than 5 Years Old

NCT00146757

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
Locations
  • Hôpital E. Herriot Lyon, France
  • Johannes Gutenberg Universität Kinderklinik, Mainz, Germany
  • Sophia Children's Hospital Rotterdam, Netherlands
  • Willink Biochemical Genetics Unit Royal Hospital for Children Manchester, United Kingdom
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Completed

Phase 3 Extension Study of the Safety and Efficacy of Aldurazyme® (Laronidase) in Mucopolysaccharidosis I (MPS I) Patients

NCT00146770

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
Locations
  • University of South Alabama Mobile, Alabama, United States
  • Emory University School of Medicine Atlanta, Georgia, United States
  • University of Rochester Rochester, New York, United States
  • University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
View all 25 locations
View Trial Details
Completed

A Study Investigating the Relationship Between the Development of Laronidase Antibody and Urinary GAG (Glycosaminoglycan) Levels in Aldurazyme® Treated Patients

NCT00144768

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
Locations
  • Childrens Hospital Los Angeles Los Angles, California, United States
  • Connecticut Children's Medical Center Hartford, Connecticut, United States
  • Children's Hospital of Wisconsin Milwaukee, Wisconsin, United States
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Active, Not Recruiting

Early Check: Expanded Screening in Newborns

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States
View Trial Details

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