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Clinical trial condition

Mucopolysaccharidosis I

Explore clinical trials studying Mucopolysaccharidosis I. Study availability and eligibility vary by location and protocol.

53 public trials 6 recruiting studies
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Mucopolysaccharidosis I trial results

Completed

Baby Detect : Genomic Newborn Screening

NCT05687474

Conditions
3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
Locations
  • CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium
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Completed

A Study of JR-171 in Patients With Mucopolysaccharidosis I

NCT04227600

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Hospital de Clínicas de Porto Alegre Porto Alegre, Brazil
  • Instituto de Genética e Erros Inatos do Metabolismo - IGEIM São Paulo, Brazil
  • Fukuoka Children's Hospital Fukuoka, Japan
View Trial Details
Completed

Efficacy and Safety of YW17 (Laronidase-CinnaGen) Compared to Aldurazyme® in MPS I Patients

NCT06406153

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Clinical Research Development Unit of Akbar Hospital, Faculty of Medicine Mashhad, Iran
  • Growth and Development Research Center, Childrens Medical Center Tehran, Iran
  • Loghman Hospital Tehran, Iran
  • Mofid Childrens Hospital Tehran, Iran
View Trial Details
Completed

Safety and Dose Ranging Study of Insulin Receptor MAb-IDUA Fusion Protein in Patients With MPS I

NCT02371226

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Emory Healthcare Decatur, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View Trial Details
Completed

Human Placental-Derived Stem Cell Transplantation

NCT01586455

Conditions
Acute Lymphocytic Leukemia, Acute Myelogenous Leukemia, Adrenal Gland Diseases, +84 more
Locations
  • Children's Hospital Colorado Denver, Colorado, United States
  • New York Medical College Valhalla, New York, United States
  • University of Utah Salt Lake City, Utah, United States
View Trial Details

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