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Clinical trial condition

Mucopolysaccharidosis I

Explore clinical trials studying Mucopolysaccharidosis I. Study availability and eligibility vary by location and protocol.

53 public trials 6 recruiting studies
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Mucopolysaccharidosis I trial results

Recruiting

MPS (RaDiCo Cohort) (RaDiCo-MPS)

NCT06036693

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +33 more
Locations
  • Centre Hospitalier Universitaire d'Angers Angers, France
  • Hôpital des Enfants - Groupe Hospitalier Pellegrin Bordeaux, France
  • Hôpital Morvan Brest, France
  • Hôpital d'Estaing Clermont-Ferrand, France
View all 23 locations
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Enrolling by Invitation

Long Term Follow-Up for RGX-111

NCT06103487

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • Children's Hospital of Orange County Orange, California, United States
  • Hospital de Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
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Completed

Mucopolysaccharidosis I (MPS I) Registry

NCT00144794

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Phoenix Children's Hospital- Site Number : 840003 Phoenix, Arizona, United States
  • Arkansas Children's Hospital- Site Number : 840109 Little Rock, Arkansas, United States
  • Southern California Permanente Medical Group- Site Number : 840108 Los Angeles, California, United States
  • USC Health Sciences Center Dept of Genetics- Site Number : 840082 Los Angeles, California, United States
View all 141 locations
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Completed

China Post-marketing Surveillance (PMS) Study of Aldurazyme®

NCT05134571

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • Investigational Site Number :1560003 Beijing, China
  • Investigational Site Number :1560002 Beijing, China
  • Investigational Site Number :1560004 Guangzhou, China
  • Investigational Site Number :1560006 Hangzhou, China
View Trial Details
Completed

An Extension Study of JR-171-101 Study in Patients With Mucopolysaccharidosis Type I (MPS I)

NCT04453085

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Hospital de Clínicas de Porto Alegre Porto Alegre, Brazil
  • Instituto de Genética e Erros Inatos do Metabolismo - IGEIM São Paulo, Brazil
  • Fukuoka Children's Hospital Fukuoka, Japan
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