NCT05073783
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Investigational Site Italy Italy
Clinical trial condition
Mucopolysaccharidosis I
Explore clinical trials studying Mucopolysaccharidosis I. Study availability and eligibility vary by location and protocol.
53 public trials
6 recruiting studies
Mucopolysaccharidosis I trial results
NCT03513328
- Conditions
- Acquired Anemia Hemolytic, Acquired Neutropenia in Newborn, Acquired Thrombocytopenia, +82 more
- Locations
-
- UF Health Shands Children's Hospital Gainesville, Florida, United States
NCT03053089
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
- Locations
-
- HCPA - Hospital das Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
Completed
Extension Study Evaluating Long Term Safety and Activity of AGT-181 in Children With MPS I
NCT03071341
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
- Locations
-
- HCPA - Hospital das Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
Completed
Safety and Dose Ranging Study of Insulin Receptor MAb-IDUA Fusion Protein in Patients With MPS I
NCT02371226
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
- Locations
-
- Children's Hospital Oakland Oakland, California, United States
- Children's Hospital of Orange County Orange, California, United States
- Emory Healthcare Decatur, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
NCT01586455
- Conditions
- Acute Lymphocytic Leukemia, Acute Myelogenous Leukemia, Adrenal Gland Diseases, +84 more
- Locations
-
- Children's Hospital Colorado Denver, Colorado, United States
- New York Medical College Valhalla, New York, United States
- University of Utah Salt Lake City, Utah, United States
NCT03406962
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +26 more
- Locations
-
- University of Minnesota Minneapolis, Minnesota, United States
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
NCT03411161
- Conditions
- Breast Diseases, Breast Neoplasms, Carbohydrate Metabolism, Inborn Errors, +17 more
- Locations
-
- Institut Jules Bordet Clinique Oncologie Médicale Brussels, Belgium
- UZ Leuven Campus Gasthuisberg Dept. of General Medical Leuven, Belgium
- Institut de Cancérologie de l'Ouest site Saint Herblain Saint-Herblain, France
- Chiba cancer center Breast surgery Chiba, Japan
NCT01173016
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
NCT01917708
- Conditions
- Albinism, Anemia, Anemia, Aplastic, +80 more
- Locations
-
- Children's Healthcare of Atlanta Atlanta, Georgia, United States