Skip to main content
OpenTrials

Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies
Refine in advanced search Browse all conditions

Lysosomal Storage Diseases trial results

Completed

A Study of Elaprase in Children and Adults With Hunter Syndrome (Mucopolysaccharidosis II) in India

NCT05058391

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • SAT Hospital - Govt Medical College Thiruvananthapuram, Kerala, India
  • JK Lone Hospital Jaipur, Rajasthan, India
  • Institute of Child Health Kolkata, India
  • All India Institute of Medical Sciences (AIIMS) New Delhi, India
View Trial Details
Completed

Long-Term Safety Follow-up Study of Cysteamine Bitartrate Delayed-release Capsules (RP103)

NCT01197378

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Disease Attributes, +8 more
Locations
  • California Pacific Medical Center (CPMC) Research Institute San Francisco, California, United States
  • Stanford University Medical School Stanford, California, United States
  • Emory Children's Center Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View Trial Details
Completed

Open-Label, Safety and Superior Effectiveness Study of Cysteamine Bitartrate Delayed-Release Capsules (RP103) in Cystinosis

NCT01733316

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Disease Attributes, +8 more
Locations
  • California Pacific Medical Center (CPMC) Research Institute San Francisco, California, United States
  • Stanford University Medical School Stanford, California, United States
  • Emory Children's Center Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View all 14 locations
View Trial Details
Completed

Phase 3 Study of Cysteamine Bitartrate Delayed-release (RP103) Compared to Cystagon® in Patients With Cystinosis

NCT01000961

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Disease Attributes, +8 more
Locations
  • Stanford University Medical School Stanford, California, United States
  • Emory Children's Center Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago (formerly Children's Memorial Hospital) Chicago, Illinois, United States
  • Hospices Civils de Lyon Lyon, France
View Trial Details

Related conditions