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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies

Lysosomal Storage Diseases trial results

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Department of Translational Medicine (DISMET) of "Federico II" University, Naples Naples, Italy
  • Children's Hospital Hacettepe University Ankara, Turkey (Türkiye)
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • University of Florida 655 W 8th St- Site Number : 8400003 Gainesville, Florida, United States
  • Metropolitan Hospital Center- Site Number : 8400001 New York, United States
  • Aurora Research Institute LLC- Site Number : 8400002 Milwaukee, Wisconsin, United States
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • UCSF Medical Center Site Number : 840005 San Francisco, California, United States
  • Emory University Site Number : 840003 Decatur, Georgia, United States
  • Montefiore Medical Center Site Number : 840006 The Bronx, New York, United States
  • Investigational Site Number : 032001 Córdoba, Argentina
View all 24 locations

NCT03292887

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • Shire Lexington, Massachusetts, United States
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
Locations
  • The Lundquist Institute at Harbor-UCLA Medical Center Torrance, California, United States
Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +8 more
Locations
  • Children's Hospital & Research Center Oakland Oakland, California, United States
  • Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center Torrance, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Peking Union Medical College Hospital Beijing, China
  • Xiangya Hospital, Central South University Changsha, China
  • West China Hospital, Sichuan University Chengdu, China
  • The Children's Hospital of Zhejiang University School of Medicine Hangzhou, China