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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies
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Lysosomal Storage Diseases trial results

Active, Not Recruiting

An Extension Study of JR-141 in Patients With Mucopolysaccharidosis Type II

NCT04348136

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
Locations
  • Fukui Clinical site Fukui, Japan
  • Fukuoka Clinical site 2 Fukuoka, Japan
  • Fukuoka Clinical site Fukuoka, Japan
  • Gifu Clinical site Gifu, Japan
View all 20 locations
View Trial Details
Active, Not Recruiting

Arrhythmia Burden, Risk of Sudden Cardiac Death and Stroke in Patients With Fabry Disease

NCT03305250

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Sydney Sydney, Australia
  • University Hospitals Birmingham NHS Foundation Trust Birmingham, West Midlands, United Kingdom
  • Cambridge University Hospitals NHS Foundation Trust Cambridge, United Kingdom
  • Cardiff and Vale University Health Board Cardiff, United Kingdom
View Trial Details
Active, Not Recruiting

Long Term Follow-up (LTFU) of Subjects Who Received SB-318, SB-913, or SB-FIX

NCT04628871

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Carbohydrate Metabolism, Inborn Errors, +24 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • New York University Grossman School of Medicine New York, United States
  • University of North Carolina Chapel Hill, North Carolina, United States
View Trial Details

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