NCT03910621
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Peking University first Hospital Beijing, China
- Xin Hua Hospital, Shanghai Jiao Tong University Shanghai, China
Clinical trial condition
Lysosomal Storage Diseases
Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.
710 public trials
130 recruiting studies
Lysosomal Storage Diseases trial results
NCT04227600
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland Oakland, California, United States
- Hospital de Clínicas de Porto Alegre Porto Alegre, Brazil
- Instituto de Genética e Erros Inatos do Metabolismo - IGEIM São Paulo, Brazil
- Fukuoka Children's Hospital Fukuoka, Japan
NCT06007768
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +22 more
- Locations
-
- Hospital Universitario Ramón y Cajal Madrid, Spain
Completed
MSOT in Pompe Disease
NCT05083806
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- University Hospital Erlangen Erlangen, Bavaria, Germany
NCT06257901
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Brunel University London London, United Kingdom
NCT04676373
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- Investigational Site China
NCT05359276
- Conditions
- Acid Sphingomyelinase Deficiency (ASMD), Brain Diseases, Brain Diseases, Metabolic, +19 more
- Locations
-
- Investigational site in France France
Completed
Miglustat in Niemann-Pick Type C Disease
NCT00517153
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
Not specified
NCT00319046
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
Not specified
NCT06801288
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- IRCCS Sant'Orsola University Hospital - Nephrology, Dialysis and Transplant Unit Bologna, BO, Italy