NCT02579239
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +10 more
- Locations
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- University of California, Irvine, ALS and Neuromuscular Center Irvine, California, United States
- Kennedy Krieger Institute; The Johns Hopkins University School of Medicine Baltimore, Maryland, United States
- OSU Wexner Medical Center Columbus, Ohio, United States
- Rigshospitalet, University of Copenhagen Copenhagen, Denmark