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Clinical trial condition

Muscular Dystrophies, Limb-Girdle

Explore clinical trials studying Muscular Dystrophies, Limb-Girdle. Study availability and eligibility vary by location and protocol.

31 public trials 5 recruiting studies

Muscular Dystrophies, Limb-Girdle trial results

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FKRP, FKRP Mutation, +17 more
Locations
  • University of California - Irvine Irvine, California, United States
  • University of Iowa Iowa City, Iowa, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
  • Kennedy Krieger Institute Baltimore, Maryland, United States
Conditions
Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Fatty Liver and Infantile-onset Cataract Caused by TRAPPC11 Mutations), Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Hypoglycosylation of Dystroglycan and Epilepsy), Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy With Hypoglycosylation of Dystroglycan), +89 more
Locations
  • Congenital Muscle Disease International Registry (www.cmdir.org) Lakewood, California, United States

NCT05206617

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Disease Progression, +11 more
Locations
  • Copenhagen Neuromuscular Center Copenhagen, Capital Region, Denmark
Active, not recruiting

LGMD R1 Natural History Study

NCT05618080

Conditions
Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
Locations
  • University of California, Irvine Orange, California, United States
  • University of Colorado Anschutz Medical Campus Aurora, Colorado, United States
  • University of Florida Gainesville, Florida, United States
  • The Community Health Clinic, Inc. Shipshewana, Indiana, United States