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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Active, Not Recruiting

Spinraza in Adult Spinal Muscular Atrophy

NCT03709784

Conditions
Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • Georgetown University Washington D.C., District of Columbia, United States
  • Johns Hopkins Baltimore, Maryland, United States
  • Massachusetts General Hospital-Harvard University Boston, Massachusetts, United States
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Active, Not Recruiting

Study to Evaluate the Safety, Tolerability, PK Characteristics and Anti-tumor Activity of FCN-159 in Adult and Pediatric Participants With Neurofibromatosis Type 1

NCT04954001

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +18 more
Locations
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • Principal Investigator Hans Gainesville, Florida, United States
  • John Hopkins All Children Hospital St. Petersburg, Florida, United States
  • Henry Ford Health System Detroit, Michigan, United States
View all 14 locations
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Active, Not Recruiting

Autism Spectrum Disorder (ASD) and Intellectual Disability (ID) Determinants in Tuberous Sclerosis Complex (TSC)

NCT02461459

Conditions
Autism Disorder, Autism Spectrum Disorder, Autistic Disorder, +23 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • University of California at Los Angeles Los Angeles, California, United States
  • Stanford University Palo Alto, California, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
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Active, Not Recruiting

FA Clinical Outcome Measures

NCT03090789

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +12 more
Locations
  • UCLA Ataxia Center Los Angeles, California, United States
  • University of Colorado Denver, Colorado, United States
  • University of Florida - Neurology Gainesville, Florida, United States
  • USF Ataxia Research Center Tampa, Florida, United States
View all 14 locations
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Active, Not Recruiting

Gene Therapy Clinical Trial for the Treatment of Leber's Hereditary Optic Neuropathy Associated With ND4 Mutations

NCT05293626

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +13 more
Locations
  • Stanford Byers Eye Institute Palo Alto, California, United States
  • University of Colorado Health Eye Center Aurora, Colorado, United States
  • Wills Eye Hospital, Neuro Ophthalmology Department Philadelphia, Pennsylvania, United States
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Active, Not Recruiting

Gene Therapy Study for Children With CLN5 Batten Disease

NCT05228145

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
Locations
  • University of Rochester Rochester, New York, United States
  • Great Ormond Street Hospital for Children London, United Kingdom
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