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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Active, Not Recruiting

A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia

NCT05515536

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +11 more
Locations
  • UCLA Los Angeles, California, United States
  • University of Florida Gainesville, Florida, United States
  • University of South Florida Tampa, Florida, United States
  • University of Iowa Iowa City, Iowa, United States
View all 14 locations
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Active, Not Recruiting

Safety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest Huntington's Disease

NCT04120493

Conditions
Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +14 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • University of Arizona (Surgical Site Only) Tucson, Arizona, United States
  • University of California, San Francisco San Francisco, California, United States
  • CenExel Rocky Mountain Clinical Research Englewood, Colorado, United States
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Active, Not Recruiting

Safety and Efficacy of TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study)

NCT06152237

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +9 more
Locations
  • Rush University Medical Center & Children's Hospital Chicago, Illinois, United States
  • Gillette Children's Specialty Healthcare Saint Paul, Minnesota, United States
  • Washington University, St. Louis St Louis, Missouri, United States
  • CHU Ste-Justine Montreal, Quebec, Canada
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Active, Not Recruiting

Open-Label Safety Study of Acoramidis (AG10) in Symptomatic ATTR Participants

NCT04988386

Conditions
Amyloid Cardiomyopathy, Transthyretin-Related, Amyloid Neuropathies, Amyloid Neuropathies, Familial, +13 more
Locations
  • Cedars-Sinai Medical Center Los Angeles, California, United States
  • University of Colorado Hospital - Anschutz Medical Campus Aurora, Colorado, United States
  • Northwestern University Chicago, Illinois, United States
  • University of Chicago Medical Center Chicago, Illinois, United States
View all 72 locations
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Active, Not Recruiting

An Open-Label Extension Study of BPN14770 in Subjects With Fragile X Syndrome

NCT05367960

Conditions
Chromosome Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
Locations
  • Amnova Clinical Research Irvine, California, United States
  • Thompson Autism & Neurodevelopment Center - CHOC Orange, California, United States
  • MIND Institute UC Davis Medical Center Sacramento, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
View all 17 locations
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