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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Active, Not Recruiting

Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab

NCT05626855

Conditions
Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
Locations
  • Phoenix Childrens Hospital Phoenix, Arizona, United States
  • UCSD Altman Clinical and Translational Research La Jolla, California, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • Stanford Neuroscience Health Center Palo Alto, California, United States
View all 49 locations
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Active, Not Recruiting

Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency:

NCT02616484

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
Locations
  • Children's Hospital of Orange County Orange, California, United States
  • Stanford University Stanford, California, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • University of Florida Gainesville, Florida, United States
View Trial Details
Active, Not Recruiting

Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi

NCT04042025

Conditions
Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +12 more
Locations
  • Stanford University Medical Center Palo Alto, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Ann Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • John Hopkins Hospital - David M. Rubenstein Child Health Building Baltimore, Maryland, United States
View all 31 locations
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Active, Not Recruiting

Open-Label Study of AG10 in Patients with Cardiomyopathy

NCT03536767

Conditions
Amyloid Cardiomyopathy, Amyloid Neuropathies, Amyloid Neuropathies, Familial, +13 more
Locations
  • Stanford University Palo Alto, California, United States
  • University of California San Francisco San Francisco, California, United States
  • Yale University New Haven, Connecticut, United States
  • Northwestern University Chicago, Illinois, United States
View Trial Details

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