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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Active, Not Recruiting

FCN-159 in Adult Patients With Symptomatic, Inoperable Neurofibromatosis Type 1-Related Plexiform Neurofibromas

NCT05913037

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +18 more
Locations
  • Cancer Hospital Chinese Academy of Medical Sciences Beijing, Beijing Municipality, China
  • Chinese Academy of Medical Sciences & Peking Union Medical College Beijing, Beijing Municipality, China
  • Plastic Surgery Hospital,Chinese Academy of Medical Sciences Beijing, Beijing Municipality, China
  • Nanfang Hospital, Southern Medical University Guangzhou, Guangdong, China
View all 15 locations
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Active, Not Recruiting

Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product

NCT02698579

Conditions
Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +24 more
Locations
  • Mattel Children's Hospital-UCLA Los Angeles, California, United States
  • Lucile Packard Children's Hospital - Stanford Palo Alto, California, United States
  • Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
  • University of Minnesota Minneapolis, Minnesota, United States
View all 13 locations
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Active, Not Recruiting

A Study of the Safety and Tolerability in Participants With PIK3CA-related Overgrowth Spectrum or Proteus Syndrome Who Are Being Treated With Miransertib (MK-7075) in Other Studies (MK-7075-006)

NCT04980872

Conditions
Bacterial Infections, Bacterial Infections and Mycoses, Congenital Abnormalities, +15 more
Locations
  • Children's Healthcare of Atlanta - Egleston Hospital ( Site 0107) Atlanta, Georgia, United States
  • Boston Children's Hospital ( Site 0089) Boston, Massachusetts, United States
  • Cincinnati Children's Hospital Medical Center-Hematology ( Site 0102) Cincinnati, Ohio, United States
  • Texas Children's Hospital ( Site 0104) Houston, Texas, United States
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Active, Not Recruiting

CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome)

NCT03566043

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
Locations
  • University of California San Francisco, Benioff Children's Hospital Oakland, California, United States
  • St. Peter's University Hospital New Brunswick, New Jersey, United States
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders Pittsburgh, Pennsylvania, United States
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Active, Not Recruiting

A Natural History Study to TRACK Brain and Spinal Cord Changes in Individuals with Friedreich Ataxia (TRACK-FA)

NCT04349514

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +11 more
Locations
  • University of Florida Gainesville, Florida, United States
  • Center for Magnetic Resonance Research, University of Minnesota Minneapolis, Minnesota, United States
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Monash Biomedical Imaging, Monash University Clayton, Victoria, Australia
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Active, Not Recruiting

A Study of NDI 1150-101 in Patients With Solid Tumors

NCT05128487

Conditions
Adenocarcinoma, Bronchial Neoplasms, Carcinoma, +36 more
Locations
  • Honor Health Research Institute Scottsdale, Arizona, United States
  • Yale Cancer Center New Haven, Connecticut, United States
  • Georgetown University Washington D.C., District of Columbia, United States
  • Ocala Oncology Center Ocala, Florida, United States
View all 19 locations
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