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Genetic Diseases, X-Linked

Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,243 public trials 227 recruiting studies

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Genetic Diseases, X-Linked trial results

Completed

An Open-Label, Single Dose Pharmacokinetic Study of Benefix (Recombinant Factor IX) in Male Chinese Subjects With Hemophilia B

NCT02213250

Conditions: Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations: Peking Union Medical College Hospital Beijing, China

Hematology Department,Beijing Children's Hospital, Capital Medical University Beijing, China

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Completed

A Study of RO4917523 in Patients With Fragile X Syndrome

NCT01517698

Conditions: Chromosome Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
Locations: Phoenix, Arizona, United States

Long Beach, California, United States

Sacramento, California, United States

Aurora, Colorado, United States

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Completed

A 6-week, Study of MG01CI Low Dose and High Dose Compared With Placebo in Adults and Adolescents With Fragile X Syndrome

NCT02126995

Conditions: Chromosome Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +14 more
Locations: Southwest Autism Research & Resource Center Phoenix, Arizona, United States

University of California Davis Pediatrics Sacramento, California, United States

Children's Hospital Colorado Aurora, Colorado, United States

RUSH University Medical Center Chicago, Illinois, United States

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Completed

A Study of Two Fabrazyme (Agalsidase Beta) Dosing Regimens in Treatment-naïve, Male Pediatric Patients Without Severe Symptoms

NCT00701415

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations: Decatur, Georgia, United States

Cincinnati, Ohio, United States

Seattle, Washington, United States

Buenos Aires, Argentina

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Completed

Evaluate the Safety and Exploratory Efficacy of GC1119

NCT01653444

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations: Asan Medical Center Songpa-gu, Seoul, South Korea

Soon Cung Hyang University Hospital Yongsan-gu, Seoul, South Korea

Ajou University School of Medicine Yeongtong-gu, Suwon, South Korea

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Completed

Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells

NCT00730314

Conditions: Agranulocytosis, Albinism, Anemia, +77 more
Locations: Children Hospital Los Angeles Los Angeles, California, United States

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Completed

Reversibility of Apixaban Anticoagulation With the Four Factor Prothrombin Complex Concentrate Kcentra

NCT02270918

Conditions: Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Cardiovascular Diseases, +11 more
Locations: Thomas Jefferson University Hosptial Philadelphia, Pennsylvania, United States

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Completed

L-citrulline and Metformin in Becker's Muscular Dystrophy

NCT02018731

Conditions: Becker's Muscular Dystrophy (BMD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +8 more
Locations: University Children's Hospital Basel, Canton of Basel-City, Switzerland

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Completed

Investigating Safety and Pharmacokinetics of 2 Different Single Doses of NNC128-0000-2011 in Haemophilia A or B Patients

NCT01288391

Conditions: Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +11 more
Locations: Berlin, Germany

Kitakyushu, Japan

Madrid, Spain

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Completed

Long-Term Follow-Up Study of Human Stem Cells Transplanted in Subjects With Connatal Pelizaeus-Merzbacher Disease (PMD)

NCT01391637

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations: UCSF Medical Center San Francisco, California, United States

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Genetic Diseases, X-Linked

Genetic Diseases, X-Linked trial results

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