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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,244 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Completed

RIXUBIS PMS India (RIXUBIS PMS)

NCT03565237

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Sahyadri Super Speciality Hospital Pune, Maharashtra, India
View Trial Details
Completed

Finding the Optimum Regimen for Duchenne Muscular Dystrophy

NCT01603407

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • University of California Los Angeles (UCLA) Medical Center Los Angeles, California, United States
  • University of California Davis Medical Center Sacramento, California, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • Nemours Children's Hospital Orlando, Florida, United States
View all 32 locations
View Trial Details
Completed

A Safety and Efficacy Extension Study of a Recombinant Fusion Protein Linking Coagulation Factor IX With Albumin (rIX-FP) in Patients With Hemophilia B

NCT02053792

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • University of Colorado Aurora, Colorado, United States
  • Indiana Hemophilia & Thrombosis Center Inc. Indianapolis, Indiana, United States
  • Hospital of the University of Pennsylvania Philadelphia, Pennsylvania, United States
  • University of Utah Salt Lake City, Utah, United States
View all 42 locations
View Trial Details
Completed

A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 (Vesleteplirsen) in Patients With Duchenne Muscular Dystrophy (DMD)

NCT03375255

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • Neuromuscular Research Center Sacramento, California, United States
  • NW FL Clinical Research Group, LLC Gulf Breeze, Florida, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View Trial Details
Completed

Clinical Study Of caNNabidiol in childrEn and adolesCenTs With Fragile X (CONNECT-FX)

NCT03614663

Conditions
Chromosome Disorders, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
Locations
  • Southwest Autism Research and Resource Center Phoenix, Arizona, United States
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • UC Davis Health System, MIND Institute Sacramento, California, United States
  • Children's Hospital of Colorado Denver, Colorado, United States
View all 21 locations
View Trial Details
Completed

Nonacog Alfa Prophylaxis And Treatment Of Bleeding Episodes In Previously Treated Patients With Hemophilia B

NCT04286412

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Nirmal Hospital Pvt Ltd. Surat, Gujarat, India
  • K.J. Somaiya Hospital and Research Centre Mumbai, Maharashtra, India
  • Sahyadri Clinical Research & Development Centre Pune, Maharashtra, India
  • Christian Medical College and Hospital Ludhiana, Punjab, India
View Trial Details

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