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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,244 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Completed

Vitamin K Antagonist Versus Direct Oral Anticoagulant Treatments in Hemophilia

NCT05804734

Conditions
Anticoagulant-induced Bleeding, Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, +9 more
Locations
  • Hemophilia treatment center of Brest Brest, France
  • Hemophilia treatment center of caen Caen, France
  • Hemophilia treatment center of Le Mans Le Mans, France
  • Hemophilia treatment center of Nantes Nantes, France
View Trial Details
Completed

Fabry Patient's Experience Of PegunigaLsidasE Alfa Monthly Infusion

NCT05186324

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • #02 Birmingham, Alabama, United States
  • #03 Atlanta, Georgia, United States
  • #04 Iowa City, Iowa, United States
  • #11 Grand Rapids, Michigan, United States
View Trial Details
Completed

A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)

NCT03439670

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • University of California Davis Davis, California, United States
  • University of California Los Angeles Los Angeles, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Nemours Children's Hospital Orlando, Florida, United States
View all 33 locations
View Trial Details
Completed

Study of Octaplex, a Four-factor Prothrombin Complex Concentrate (4F-PCC) and Beriplex® P/N (Kcentra) for the Reversal of Vitamin K Antagonist (VKA) Induced Anticoagulation in Patients Needing Urgent Surgery With Significant Bleeding Risk.

NCT02740335

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
Locations
  • Octapharma Research Site Aurora, Colorado, United States
  • Octapharma Research Site New Haven, Connecticut, United States
  • Octapharma Research Site Miami, Florida, United States
  • Octapharma Research Site Tampa, Florida, United States
View all 86 locations
View Trial Details
Completed

Natural History of the Progression of Choroideremia Study

NCT03359551

Conditions
Choroid Diseases, Choroideremia, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +8 more
Locations
  • Research Site Los Angeles, California, United States
  • Research Site Miami, Florida, United States
  • Research Site Baltimore, Maryland, United States
  • Research Site New York, United States
View all 20 locations
View Trial Details
Completed

Clinical Study to Evaluate the Efficacy and Safety of Givinostat in Ambulant Patients With Duchenne Muscular Dystrophy

NCT02851797

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Neuromuscular Research Center UC Davis Department of Physical Medicine and Rehabilitation Davis, California, United States
  • Rady Children's Hospital center - UCSD Department of Neuroscience San Diego, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Connecticut Children's Medical Center - Division Neurology Hartford, Connecticut, United States
View all 42 locations
View Trial Details
Completed

ATHN 8: Previously Untreated Patients (PUPs) Matter Study

NCT03818529

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +14 more
Locations
  • Arizona Hemophilia and Thrombosis Center at Phoenix Children's Hospital Phoenix, Arizona, United States
  • Valley Children's Hospital Madera, California, United States
  • Rady Children's Hospital San Diego San Diego, California, United States
  • UCSF Pediatric Hemophilia Treatment Center at Mission Bay San Francisco, California, United States
View all 27 locations
View Trial Details

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