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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,244 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Completed

A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)

NCT05096221

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Little Rock, Arkansas, United States
  • UC San Diego Altman Clinical and Translational Research Institute La Jolla, California, United States
  • UCLA Medical Center Los Angeles, California, United States
  • Lucile Packard Children's Hospital at Stanford Palo Alto, California, United States
View all 42 locations
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Completed

Study of Long Term Safety and Clinical Outcomes of Idursulfase IT and Elaprase Treatment in Pediatric Participants Who Have Completed Study HGT-HIT-094

NCT02412787

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • Children's Hospital and Research Center at Oakland Oakland, California, United States
  • Ann & Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • University of North Carolina Chapel Hill, North Carolina, United States
  • Women's and Children's Hospital Adelaide, Australia
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Completed

Study of the Efficacy and Safety PF-06741086 in Adult and Teenage Participants With Severe Hemophilia A or Moderately Severe to Severe Hemophilia B

NCT03938792

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +11 more
Locations
  • USF Health Morsani Center For Advanced Healthcare Tampa, Florida, United States
  • University of Iowa Iowa City, Iowa, United States
  • Northwell Health HTC New Hyde Park, New York, United States
  • Washington Institute for Coagulation Seattle, Washington, United States
View all 62 locations
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