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Clinical trial condition

Genetic Diseases, X-Linked

Explore clinical trials studying Genetic Diseases, X-Linked. Study availability and eligibility vary by location and protocol.

1,243 public trials 227 recruiting studies
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Genetic Diseases, X-Linked trial results

Completed

Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector

NCT01129544

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, Genetic Diseases, Inborn, +9 more
Locations
  • Mattel Children's Hospital - UCLA Los Angeles, California, United States
  • Children's Hospital Boston Boston, Massachusetts, United States
  • Cincinnati Children's Medical Center Cincinnati, Ohio, United States
View Trial Details
Completed

DMD- Interactive Virtual Reality Study

NCT06274983

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Sheffield Childrens NHS FT Sheffield, South Yorkshire, United Kingdom
View Trial Details
Completed

Dose-Ranging Study of ST-920, an AAV2/6 Human Alpha Galactosidase A Gene Therapy in Subjects With Fabry Disease (STAAR)

NCT04046224

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of California, Irvine Irvine, California, United States
  • University of South Florida Tampa, Florida, United States
  • Emory University School of Medicine Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View all 18 locations
View Trial Details
Completed

Darolutamide in Patients With Androgen Receptor-Positive Salivary Gland Carcinoma (DISCOVARY)

NCT05694819

Conditions
Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +18 more
Locations
  • Nagoya University Hospital Nagoya, Aichi-ken, Japan
  • Chiba University Hospital Chiba, Japan
  • National Cancer Center Hospital East Kashiwa, Chiba, Japan
  • National Hospital Organization Kyushu Medical Center Fukuoka, Japan
View Trial Details
Completed

Dose-Escalation Study Of A Self Complementary Adeno-Associated Viral Vector For Gene Transfer in Hemophilia B

NCT00979238

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +7 more
Locations
  • Stanford Medical School Stanford, California, United States
  • St. Jude Children's Research Hospital Memphis, Tennessee, United States
  • Scott and White Memorial Hospital Temple, Texas, United States
  • Katharine Dormandy Haemophilia Centre and Haemostasis Unit, University College of London London, United Kingdom
View Trial Details
Completed

Long-term Evaluation on Height and Weight in Patients With MPS II Who Started Treatment at < 6 Years of Age

NCT02455622

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Hospital Infantil Dr Robert Reid Cabral Santo Domingo, Dominican Republic
  • Universitätsmedizin der Johannes Gutenberg-Universität Mainz Mainz, Germany
  • Hospital Kuala Lumpur Kuala Lumpur, Malaysia
View Trial Details
Completed

HOPE-B: Trial of AMT-061 in Severe or Moderately Severe Hemophilia B Patients

NCT03569891

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +11 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Los Angeles Orthopedic Hospital Los Angeles, California, United States
  • Children's Hospital of Los Angeles Los Angeles, California, United States
View all 33 locations
View Trial Details

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